Duchenne research
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Distrofia di Duchenne, le ricerche sul farmaco sperimentale SMTC 1100

Intervista al Prof. Francesco Muntoni, Dubowitz Neuromuscular Centre, UCL Institute of Child Health, London, UK

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Imaging DMD

Imaging DMD | Duchenne research | Scoop.it

Patrick was 8 years old. Steroids were not recommended. There was no imaging and no way to predict his loss of ambulation. Sure, he fell occasionally. Some day…

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WCRS Holds Duchenne Dash Photography Exhibition | LBBOnline

WCRS Holds Duchenne Dash Photography Exhibition  | LBBOnline | Duchenne research | Scoop.it

Little Black Book,
24-hour London to Paris charity cycle ride aids charity 'Duchenne Children's Trust

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Ten-year-old campaigner vows to keep fighting for others after award win - Bucks Free Press

Ten-year-old campaigner vows to keep fighting for others after award win - Bucks Free Press | Duchenne research | Scoop.it
Archie Hill, who has Duchenne muscular dystrophy, was rewarded for his “tireless” campaigning with the title of Most Inspirational campaigner…
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Dance competition raises money for Duchenne Muscular Dystrophy research - WBFO

Dance competition raises money for Duchenne Muscular Dystrophy research - WBFO | Duchenne research | Scoop.it
It was just like "Dancing with the Stars" at Statler City Friday night. Suneel's Light Foundation held its third annual fund-raising gala that features
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LeBron sends touching letter to teen with Duchenne muscular dystrophy - ESPN

LeBron sends touching letter to teen with Duchenne muscular dystrophy - ESPN | Duchenne research | Scoop.it
LeBron James sent an inspiring message to 19-year-old Emanuel Duncan: "Together we will change the world."
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FDA fast-tracks drug to treat Duchenne muscular dystrophy

FDA fast-tracks drug to treat Duchenne muscular dystrophy | Duchenne research | Scoop.it
WASHINGTON — A drug that has been helping a Pittsburgh-area boy in a clinical trial defy the odds in battling a form of muscular dystrophy is a step closer to going to market.
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Risks in a Trial of an Innovative Treatment of Duchenne Muscular Dystrophy - AAP News

Risks in a Trial of an Innovative Treatment of Duchenne Muscular Dystrophy
AAP News
Studies of innovative therapies for muscular dystrophy raise unique ethical issues. The disease is currently untreatable and relentlessly progressive.
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Santhera Reports New Data and Updates on Regulatory Filings for Raxone ... - Nasdaq

Santhera Reports New Data and Updates on Regulatory Filings for Raxone ... - Nasdaq | Duchenne research | Scoop.it
Santhera Pharmaceuticals Holding AG / Santhera Reports New Data and Updates on Regulatory Filings for Raxone® in Duchenne Muscular Dystrophy ..
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FDA grants Marathon Pharma's DMD candidate deflazacort rare pediatric disease ... - Seeking Alpha

The FDA grants rare pediatric disease designation for privately held Marathon Pharmaceuticals' deflazacort for the treatment of Duchenne muscular dystrophy
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Sarepta Unveils New Data to Make Stronger Case for Duchenne Drug Approval - TheStreet.com

Sarepta Unveils New Data to Make Stronger Case for Duchenne Drug Approval - TheStreet.com | Duchenne research | Scoop.it
Sarepta (SRPT) hopes the new data will convince FDA to approve eteplirsen as a new treatment for Duchenne early next year.. Sarepta Therapeutics Inc(SRPT)
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Human α7 Integrin Gene (ITGA7) Delivered by Adeno-Associated Virus Extends Survival of Severely Affected Dystrophin/Utrophin-Deficient Mice

Human α7 Integrin Gene (ITGA7) Delivered by Adeno-Associated Virus Extends Survival of Severely Affected Dystrophin/Utrophin-Deficient Mice | Duchenne research | Scoop.it
RT @MayoClinicPMR: MT @LiebertPub Human α7 Integrin Gene Extends Survival of Dystrophin/Utrophin-Deficient Mice
http://t.co/SNVYmoQbAn #m…
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ReveraGen BioPharma (VBP15) [PPMD's 2015 Connect Conference]

Speakers: Eric Hoffman, PhD.
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FDA rejects PTC's application for muscular dystrophy drug - PMLiVE

FDA rejects PTC's application for muscular dystrophy drug - PMLiVE | Duchenne research | Scoop.it

Says Translarna filing not “sufficiently complete” to
permit full review

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New hope for Prosensa’s drisapersen

New hope for Prosensa’s drisapersen | Duchenne research | Scoop.it

New data suggest that Prosensa’s DMD drug drisapersen may work in a subgroup despite a failed Phase III study.

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Duchenne muscular dystrophy affects stem cells, University of Ottawa study finds - CBC.ca

Duchenne muscular dystrophy affects stem cells, University of Ottawa study finds - CBC.ca | Duchenne research | Scoop.it
New treatments could one day be available for the most common form of muscular dystrophy after a Univeristy of Ottawa and Ottawa Hospital study suggests the debilitating genetic disease affects the stem cells that produce healthy muscle fibres.
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'Ringo the dog' Helps Find Potential New Therapy for Muscular Dystrophy - Muscular Dystrophy News

'Ringo the dog' Helps Find Potential New Therapy for Muscular Dystrophy - Muscular Dystrophy News | Duchenne research | Scoop.it
Read more about the dog with a mutation on gene Jagged1 that inhibits muscular dystrophy effects leading to a potential new therapy for DMD
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BLOG to help fundraise for Duchenne's - Hastings and St. Leonards Observer

BLOG to help fundraise for Duchenne's - Hastings and St. Leonards Observer | Duchenne research | Scoop.it
Battle Light Opera Group (BLOG) will be bring Gilbert and Sullivan’s ‘The Mikado’ to Battle’s Memorial Halls under the directorship of Sue Gladman and the baton of Andrew J Daniels.
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Genetic Target for Treating Duchenne Muscular Dystrophy Identified - Neurology Advisor

Genetic Target for Treating Duchenne Muscular Dystrophy Identified - Neurology Advisor | Duchenne research | Scoop.it
Researchers have linked the Jagged1 gene to a much milder form of muscular dystrophy in golden retrievers.
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Action Duchenne Conference 2015 Sibs Mockumentary: the boys group

Check out this fantastic short documentary made by siblings of boys with Duchenne at this year's Action Duchenne Conference with the help of Liza Tercero and ...
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Boys with Duchenne muscular dystrophy denied breakthrough drug - ITV News

Boys with Duchenne muscular dystrophy denied breakthrough drug - ITV News | Duchenne research | Scoop.it
The National Institute for Health and Care Excellence has announced it will not recommend funding on the NHS for breakthrough drug Translarna which could keep boys with life-limiting Duchenne muscular dystrophy walking for longer.
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Santhera plans for US and EU approval filing of Raxone for DMD - The Pharma Letter (registration)

Santhera plans for US and EU approval filing of Raxone for DMD - The Pharma Letter (registration) | Duchenne research | Scoop.it
Santhera plans for US and EU approval filing of Raxone for DMD
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Parent Project Muscular Dystrophy Launches Next Phase of Genetic Testing ... - MarketWatch

Parent Project Muscular Dystrophy Launches Next Phase of Genetic Testing ... - MarketWatch | Duchenne research | Scoop.it
TheStreet.com
Parent Project Muscular Dystrophy Launches Next Phase of Genetic Testing ...
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Sodium nitrate alleviates functional muscle ischemia in patients with Becker muscular dystrophy - Nelson - The Journal of Physiology - Wiley Online Library

New #JPhysiol. paper from Ron Victor's lab on sodium nitrate treatement alleviates muscle ischemia in BMD patients http://t.co/nSMyoZ0K51
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PPMD Announces Launch of Next Phase Decode Duchenne Genetic Testing Program - Muscular Dystrophy News

PPMD Announces Launch of Next Phase Decode Duchenne Genetic Testing Program - Muscular Dystrophy News | Duchenne research | Scoop.it
Read more about PPMD announces Launch of Next Phase Decode Duchenne genetic testing program
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