Rare Diseases - Orphan drugs
81 views | +0 today
Follow
Rare Diseases - Orphan drugs
We scoop here all relevant articles/news/video/... about rare diseases or orphan drugs
Your new post is loading...
Your new post is loading...
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Rare Disease Day, 28 Feb 2013

Rare Disease Day, 28 Feb 2013 | Rare Diseases - Orphan drugs | Scoop.it
February 28, 2013 marks the sixth international Rare Disease Day coordinated by EURORDIS and organised with rare disease national alliances in 24 European co...
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: Ombrabulin, for the: Treatment of soft tissue sarcoma

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: Porfimer sodium (for use with photodynamic therapy), for the: Treatment of cholangiocarcinoma

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

EvaluatePharma Orphan Drug Report 2013

EvaluatePharma Orphan Drug Report 2013 | Rare Diseases - Orphan drugs | Scoop.it
free #orphan drug report 2013 http://t.co/AyvIYCi0p5
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: Lenvatinib, for the: Treatment of follicular thyroid cancer

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: 4-[2-(6-methylpyridin-2-yl)-5,6-dihydro-4H-pyrrolo[1,2-b]pyrazol-3-yl]-quinoline-6-carboxamide monohydrate, for the: Treatment of glioma

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: Nintedanib, for the: Treatment of idiopathic pulmonary fibrosis

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Purchases of Orphan Drug to Treat Hormone Deficiency Limited

Ipsen BioPharma's #OrphanDrug Increlex to Treat Hormone Deficiency Is Limited Due to imminent halt in production http://t.co/doM5vsPw4H
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Twitter / saraenichols: Rare disease info in special ...

Twitter / saraenichols: Rare disease info in special ... | Rare Diseases - Orphan drugs | Scoop.it
RT @saraenichols: Rare disease info in special report from @lisamjarvis @cenmag http://t.co/WrsX5uBkia
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: Bosutinib, for the: Treatment of chronic myeloid leukaemia

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

The Rare Disease Search Engine That Outperforms Google | MIT Technology Review

The Rare Disease Search Engine That Outperforms Google | MIT Technology Review | Rare Diseases - Orphan drugs | Scoop.it
A powerful new search engine designed to help diagnose rare diseases could prove a boon for both medics and the public
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Rare Disease Day 2013 - Feb 28

Rare Disease Day 2013 - Feb 28 | Rare Diseases - Orphan drugs | Scoop.it
This year, RaDiOrg.be will use the symbol of Rare Disease Day 2013 to officially launch the process of the organization of the EUROPLAN conference in Belgium (2014) by organizing, on the 28th of February 2013, the EUROPLAN steering committee’s...
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Social Media Transforming Care for Rare Disease Patients | HealthWorks Collective

Social Media Transforming Care for Rare Disease Patients | HealthWorks Collective | Rare Diseases - Orphan drugs | Scoop.it
Social media is transforming care for rare disease patients in three ways: facilitating diagnosis, connecting patients with treatments and helping create additional funding sources for new therapies.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Rare Disorders without Borders - XUJPRSM1

Rare Disorders without Borders - XUJPRSM1 | Rare Diseases - Orphan drugs | Scoop.it
In celebration of RARE DISEASE WEEK 2013, Xavier University- Dr. Jose P. Rizal School of Medicine...
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: Rifapentine, for the: Treatment of tuberculosis

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Report: Orphan Drugs Offer Good Return on Investment

Report: Orphan Drugs Offer Good Return on Investment | Rare Diseases - Orphan drugs | Scoop.it
EvaluatePharma’s first-ever report covering the orphan disease sector predicted that the orphan drug market will reach $127 billion by 2018 and will grow at a rate that is nearly twice that of the overall prescription drug market.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: R,S-O-(3-piperidino-2-hydroxy-1-propyl)-nicotinic acid amidoxime dihydrochloride, for the: Treatment of Duchenne muscular dystrophy

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: Lenvatinib, for the: Treatment of papillary thyroid cancer

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: 2-Hydroxypropyl-β-cyclodextrin, for the: Treatment of Niemann-Pick disease type C

European Union agency responsible for the protection of public and animal health through the scientific evaluation and supervision of medicines.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Leveling the Playing Field in Orphan Drug Development | Trials Without Tribulations

Leveling the Playing Field in Orphan Drug Development | Trials Without Tribulations | Rare Diseases - Orphan drugs | Scoop.it
Trials of orphan drugs often involve smaller sample sizes. How much smaller? Cut the typical phase 3 sample size by 75% and then, for many orphan trials, c... (How big a sample size will you need for a pivotal trial of your orphan drug?
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Ipsen warns of shortages of its orphan drug Increlex | Global Regulatory Science

Eric Palmer French drugmaker Ipsen says shortages of its orphan drug Increlex appear inevitable because of ongoing ...http://t.co/70GPsy7jwp
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

3-D printer helps save dying baby with rare disease

3-D printer helps save dying baby with rare disease | Rare Diseases - Orphan drugs | Scoop.it
A baby boy in Ohio with a rare respiratory condition is alive, thanks in large part to a device made by a 3-D printer.
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Orphan designation: Zoledronic acid, for the: Treatment of complex regional pain syndrome

On 6 February 2013, the Committee for Orphan Medicinal Products (COMP) adopted a negative opinion on the orphan designation application for zoledronic acid for the treatment of complex regional pain syndrome (CRPS).
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Pharmaceutical, medical, clinical, scientific and development jobs | NextPharmaJob.com

drug development jobs
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

Bayer’s Orphan Drug Stivarga Receives A Second FDA Indication

Bayer’s Orphan Drug Stivarga Receives A Second FDA Indication | Rare Diseases - Orphan drugs | Scoop.it
On February 25, 2013, Bayer and Onyx Pharmaceuticals announces that the US FDA approves orphan drug Stivarga (Regorafenib) tablets for the treatment of patients with locally advanced, unresectable ...
more...
No comment yet.
Scooped by MediPlanet / PharmaPlanet
Scoop.it!

EURORDIS honours Genzyme with rare disease company award | pharmaphorum

EURORDIS honours Genzyme with rare disease company award | pharmaphorum | Rare Diseases - Orphan drugs | Scoop.it
This is a pharma news story about EURORDIS who have honoured Sanofi’s Genzyme with a company award for its work in rare diseases.
more...
No comment yet.